Experimental compound displays effectiveness in treating symptoms of Autism and Alzheimer’s disease

Experimental compound, which has received orphan drug and pediatric rare disease designations from the FDA, displays effectivene
Prof. Illana Gozes. Credit: Jonathan Blum, Tel Aviv University.

An extensive international study led by Tel Aviv University found that an experimental drug which has been awarded orphan drug designation by the FDA for future treatment of a rare development disorder can also treat a variety of symptoms relating to autism, intellectual disability, and Alzheimer’s disease.

The experimental drug, NAP, was discovered in the lab of Prof. Illana Gozes of the Tel Aviv University Sackler Medical School’s Department of Human Molecular Genetics and Biochemistry. In recent years, the FDA has granted the experimental drug with orphan drug designation and pediatric rare…

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